Gene Therapy for HD

Nature news reports the encouraging news from a gene therapy trial for Huntington's Disease:

A one-time gene therapy can markedly slow the progression of Huntington’s disease, potentially paving the way for the first ever treatment to alter the course of this rare, inherited brain disorder.

In a small trial of 29 people who were in the early stages of Huntington’s-related decline, participants who received a high dose of the therapy directly into their brains saw the disease slow by 75% over three years, compared with those in a control group.

Cheers, 

Colin